Categories for Research News

Positive Update from Vamorolone Trial

June 7, 2021 12:47 pm

Steriods are the main stay treatment for those living with Duchenne, Alex has been on them since he was 4, they come with lots of nasty side effects, including poor bone health – Alex broke his hip when he was just 9 years old.As...

#CTD2021

May 20, 2021 9:34 am

Today is Clinical Trials Day, the work we do at Alex’s Wish is to fund clinical trials that will hopefully one day see Duchenne cured for good! ...

Alex meets Marianela Schiava

January 20, 2021 2:38 pm

The last time that Alex visited Newcastle he was so pleased to be able to meet Marianela Schiava. Marianela is the Clinical Research Associate, a position that Alex’s Wish funded £30,000 towards, alongside Duchenne UK....

Gene Therapy Update

January 13, 2021 10:53 am

This is exciting news for all affected by Duchenne. Gene therapy cannot come soon enough it’s one of the things we are all working so hard to get....

Thank you and Merry Christmas

December 17, 2020 1:39 pm

As we near the end of 2020, we’ve been reflecting on what’s been achieved together.  We started the year with huge plans, with the momentum that we had established we were sure that this would be our most successful year yet! ...

Update on Vamorolone Study

October 7, 2019 9:11 am

Top Line Data of 18-month Vamorolone treatment of Duchenne Muscular Dystrophy patients shows continued improvement of symptoms with reduction in Corticosteroid safety concerns....

Solid Bioscience Gene Therapy Update

August 19, 2019 8:49 am

Alex’s Wish have received a positive update from Solid Bioscience on their gene therapy trial called IGNITE DMD which Alex’s Wish invested in....

End of Year Update from Emma

December 20, 2018 9:07 pm

As 2018 comes to end, I wanted to share with you an update on how this year has gone. For a start, it’s been our best year in terms of fundraising....

Update on Gene Therapy

July 3, 2018 12:53 pm

In recent years, our community has watched with hope as pre-clinical data has emerged showing the promise of gene therapy as a valuable treatment for everyone living with Duchenne Muscular Dystrophy. ...

Alex’s Wish gives £50,000 grant to Solid-GT

October 15, 2016 7:53 am

Alex’s Wish partners with Solid-GT and funds important Gene Therapy Development We would like to thank all of our supporters who have enabled us to give a £50,000.00 grant to Solid-GT to support their Gene Therapy Development....

First genetic cure for rare diseases!

April 28, 2015 11:41 am

New era of medicine begins as first children cured of genetic disorder The pioneering therapy offers hope to the hundreds thousands of people suffering from inherited conditions This story gives hope to boys living with Duchenne Muscular Dystrophy....