Categories for Research News

Update on Vamorolone Study

October 7, 2019 9:11 am

Top Line Data of 18-month Vamorolone treatment of Duchenne Muscular Dystrophy patients shows continued improvement of symptoms with reduction in Corticosteroid safety concerns....

Solid Bioscience Gene Therapy Update

August 19, 2019 8:49 am

Alex’s Wish have received a positive update from Solid Bioscience on their gene therapy trial called IGNITE DMD which Alex’s Wish invested in....

End of Year Update from Emma

December 20, 2018 9:07 pm

As 2018 comes to end, I wanted to share with you an update on how this year has gone. For a start, it’s been our best year in terms of fundraising....

Update on Gene Therapy

July 3, 2018 12:53 pm

In recent years, our community has watched with hope as pre-clinical data has emerged showing the promise of gene therapy as a valuable treatment for everyone living with Duchenne Muscular Dystrophy. ...

Alex’s Wish gives £50,000 grant to Solid-GT

October 15, 2016 7:53 am

Alex’s Wish partners with Solid-GT and funds important Gene Therapy Development We would like to thank all of our supporters who have enabled us to give a £50,000.00 grant to Solid-GT to support their Gene Therapy Development....

First genetic cure for rare diseases!

April 28, 2015 11:41 am

New era of medicine begins as first children cured of genetic disorder The pioneering therapy offers hope to the hundreds thousands of people suffering from inherited conditions This story gives hope to boys living with Duchenne Muscular Dystrophy....