Gene Therapy UpdateJanuary 13, 2021 10:53 am
This is exciting news for all affected by Duchenne. Gene therapy cannot come soon enough it’s one of the things we are all working so hard to get.
Brenda Cooperstone, MD, Chief Development Officer, Rare Disease, Pfizer Global Product Development. “We believe our gene therapy candidate, if successful in Phase 3 and approved, has the potential to significantly improve the trajectory of DMD disease progression, and we are working with worldwide regulatory authorities to initiate this program as quickly as possible in other countries.”
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