Positive Update from Vamorolone Trial

June 7, 2021 12:47 pm

Steriods are the main stay treatment for those living with Duchenne, Alex has been on them since he was 4, they come with lots of nasty side effects, including poor bone health – Alex broke his hip when he was just 9 years old.As a Charity, we wanted to support a project to help bring a new drug to market that will hopefully one day replace steriods with something that works just as well but has far less side effects.

We invested £47,000 into Vamorolone with Eric Hoffman, CEO at ReverGen back in 2015 and we have just received positive news, Vamorolone demonstrates strong efficacy across primary and secondary endpoints!!!This is such great news for the Duchenne community and for those children and young adults living with this condition.

Read more from the official press release here

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