Tag Archive: Duchenne

Two new Trustees join the Board at Alex’s Wish.

April 12, 2024 10:22 am

We are so pleased to announce that we have successfully appointed two new Trustees to join our Board. Dr Aishah Iqbal and William Hazlerigg join their fellow Trustees from the 1st of April....

Fill our Hearts with Hope

February 15, 2024 4:08 pm

February is the month of LOVE, so what a perfect time to launch our HEART campaign….. Our heart muscles need dystrophin to function efficiently....

Sunday Spotlight – Meet ‘Team Swepstone’

October 27, 2023 11:09 am

For those that don’t know you, how would you describe yourself and your situation? I was diagnosed with Meniere’s Disease 20 years ago, and over that time have had to deal with violent vertigo attacks and progressive hearing loss in both ears....

Autumn Lunch

October 12, 2023 11:22 am

Collaboration : “Alone we can do so little; together we can do so much” What an incredible afternoon we had on Friday, 6th October at our Alex’s Wish Annual Autumn Lunch at The Novotel Hotel in Leicester....

Our fantastic Miss Great Britain’s

October 2, 2023 12:18 pm

The support shown for Alex’s Wish by the Miss Great Britain, Ms Great Britain and Ms Great Britain Classic finalists clearly shows that their beauty extends far beyond good looks....

Golf Day 2023 raises over £12,000

September 25, 2023 4:04 pm

A huge thanks to everyone that came along to support Alex’s Wish Golf Day! What a great day – fabulous sunshine with a teeny tiny amount of rain, great company and we raised over £12,000 – amazing!!...

Fabulous FrontlineFormula 1 Event

August 31, 2023 2:29 pm

An amazing race day took place at the Frontline Recruitment Group Grand Prix yesterday – raising £1,300! Thank you so much to everyone that cam along and took part!...

Right Royal Weekend!

June 19, 2023 2:36 pm

Emma, our founder and Alex’s Mum had a fabulous weekend around the Kings Coronation. Emma was lucky enough to go to the King’s Coronation Concert and then just a few days later went to the King’s garden party....

Alex’s Wish Spring Launch 2023

March 20, 2023 1:47 pm

Our Spring Launch took place at the Novotel in Leicester on 17th March, sponsored by Janine Edwards Wealth Management and Spirit Healthcare....

Today, 28th February marks #RareDiseaseDay.

February 28, 2023 9:43 am

Duchenne Muscular Dystrophy is a rare disease. A condition that affects 1 in every 3,500 boys born. Alex was diagnosed with this condition shortly before his 4th birthday....

Supercar Day Success

July 29, 2022 12:54 pm

Supercars 2022 raises £12,120 for Alex’s Wish This year’s Alex’s Wish annual Supercars event was another resounding success, raising a wonderful £12,120 for the Leicestershire-based Duchenne charity....

Italfarmaco announces positive topline data from Phase 3 trial showing positive benefits of Givinostat in Duchenne

July 4, 2022 1:10 pm

Italfarmaco Group Announces Positive Topline Data from Phase 3 Trial Showing Beneficial Effect of Givinostat in Patients with Duchenne Muscular Dystrophy  — Study meets primary endpoint with secondary and exploratory endpoints showing consistency with primary endpoint —  — Data reinforces previously observed safety profile for Givinostat; treatment in boys with DMD continues to show a good tolerability profile —  — The company is planning to discuss the potential for marketing application submission with regulatory authorities for Givinostat in DMD —  — Results were presented at the Annual PPMD Conference on June 25, 2022 —  MILAN, Italy, June 25, 2022 – Italfarmaco Group announced today positive topline data from its completed Phase 3 EPIDYS trial with Givinostat, the company’s proprietary histone deacetylase (HDAC) inhibitor, in boys with Duchenne Muscular Dystrophy (DMD)....