We were thrilled to hear the news last Friday, that NICE have given the green light on Translarna – the first ever drug to treat the underlying cause of Duchenne for those eligible. ...
We would like to thank Rachel Hargraves from RDZ-PR who is donating her time to Alex’s Wish – a true Wish Warrior – to raise awareness of our cause....
On Wednesday, 11th February, Alex’s Wish took part in a vigil at the door of the NHS England alongside a number of Duchenne charities, families and supporters to demand access to a new ground-breaking drug Translarna. ...
Patients with Duchenne Muscular Dystrophy have been specifically disadvantaged by the failure of the NHS England system to consider funding drugs for rare diseases....
Alex’s Wish took part in a lobby at Westminster on Wednesday, 14th January with the aim to ensure early availability and full funding of a pioneering new treatment called Translarna....
