Tag Archive: NICE

First Treatment for all patients with Duchenne approved

December 13, 2024 3:29 pm

This week we received THE BEST NEWS the first treatment for EVERYONE living with Duchenne has been approved!!!!  NICE, the National Institute of Clinical Excellence in England and Wales announced that Agamree (also known as Vamorolone) a dissociative steroid, has been approved for ALL patients with Duchenne Muscular Dystrophy....

Alex’s Wish attends Health & Technology Workshop

September 16, 2016 12:21 pm

We were delighted to attend a workshop organised by Duchenne UK this week in London. The workshop was designed to understand the Health Technology Assessment (HTA) process in England, and to give an overview of health economics and the process of new drug approval and how the Duchenne community can come together to bring new drugs to market as quickly as possible....