Thank you!!
With your support, Alex’s Wish – Cure Duchenne has been able to give £280K towards vital projects to benefit the Duchenne community in 2025. Here’s a snapshot of our impact this year: ◼£200K given to a new Innovative Medical Grant Call, investing in medical research is vital if we are to be able to offer […]
Alex’s Wish funds £200,000 towards Duchenne UK award of £500,000 to accelerate development of gene editing therapy for Duchenne muscular dystrophy
We are proud to announce that thanks to our incredible supporters we were able to fund £200,000 of the £500,000 in funding for MyoGene Bio, a San Diego-based biotech company, to support the development of an innovative gene editing therapy for Duchenne muscular dystrophy (DMD). Therapeutic Call The funding is the result of Duchenne UK’s […]
Givinostat – Early Access Scheme – the fight continues for patients to gain access
Alex has been taking part in clinical trials most of his life – 9 years in fact. We are so grateful this has been the case, when Alex was diagnosed with Duchenne at 3 years old – there were no trials available for us to even consider. The purpose of taking part in clinical trials […]
Early Access Programme for Givinostat
We’ve been talking about Givinostat for some time now especially at our events.This is a new drug that Alex has been on for the past 5 years, that is proving to be delaying disease progression.It’s currently going through the NICE approval process, but as with these things it’s a slow process – all while families […]
Abseil Challenge 2024
Six incredible people decided to take on the Northampton Lift Tower and a 418 foot abseil for Alex’s Wish. We were lucky with the weather, although some of the six may dispute that, secretly hoping it may be cancelled!! Everyone overcame all their fears and completed the challenge – it was incredible watching them all […]
Study paves the way for improved detection of heart disease in female carriers of DMD
A recent report from a study funded by partly by Alex’s Wish, in collaboration with Duchenne UK has improved understanding of early detection of heart muscle disease in female carriers of Duchenne muscular dystrophy (DMD), paving the way for further research. Women and girls who carry a mutated DMD gene (‘carriers’) can sometimes show mild symptoms of the […]
Alex’s Wish pledges £20,000 to Duchenne UK’s gene therapy grant call
Alex’s Wish has pledged £20,000 so far towards a £1 million grant call into treatments which will ultimately allow everyone living with Duchenne Muscular Dystrophy to receive gene therapy safely and effectively. Alex’s Wish are also hoping to pledge another £80,000 over the early Autumn months to support this project from their fundraising activities over […]
Super media coverage
We would like to thank Rachel Hargraves from RDZ-PR who is donating her time to Alex’s Wish – a true Wish Warrior – to raise awareness of our cause. Through this relationship we have generated a great deal of media coverage in the last week across the Leicestershire region in both the Leicester Mercury and Loughborough Echo. We now […]
Urgent Call to Action – Translarna
Patients with Duchenne Muscular Dystrophy have been specifically disadvantaged by the failure of the NHS England system to consider funding drugs for rare diseases. England was a leader in the trials for Translarna, in keeping with the government strategy to promote innovation and inward investment in trials. Just 80 patients might benefit from this drug […]
What a successful first year…
Alex’s Wish has been up and running for a year now – and what a year it has been! To date, we have raised over £60,000 to be invested in new clinical trials and research projects to help all children living with Duchenne. From The Big Buggy Push event held just a few weeks ago […]