Gene Therapy

This project has been funded by the following charities:

Project leader: Professor George Dickson
Location: Royal Holloway (University of London)
Conditions: Duchenne muscular dystrophy; Becker muscular dystrophy
Duration: Three years, starting 2013
Total project cost: £ 180,306
Official title: Development of dual/triple transpliced AAV vectors to restore quasi/full length dystrophin variants to muscle.