This week we received THE BEST NEWS the first treatment for EVERYONE living with Duchenne has been approved!!!! NICE, the National Institute of Clinical Excellence in England and Wales announced that Agamree (also known as Vamorolone) a dissociative steroid, has been approved for ALL patients with Duchenne Muscular Dystrophy....
We’ve been talking about Givinostat for some time now especially at our events.This is a new drug that Alex has been on for the past 5 years, that is proving to be delaying disease progression.It’s...
EMA recommends approval of first ever treatment for all DMD patients Today The European Medicines Agency (EMA) has recommended the approval of Vamorolone, the first ever treatment for all patients with Duchenne muscular dystrophy (DMD)....
We were delighted to attend a workshop organised by Duchenne UK this week in London. The workshop was designed to understand the Health Technology Assessment (HTA) process in England, and to give an overview of health economics and the process of new drug approval and how the Duchenne community can come together to bring new drugs to market as quickly as possible....
