Categories for Drug approval process

Great news for the Duchenne Community

October 14, 2023 11:02 am

EMA recommends approval of first ever treatment for all DMD patients Today The European Medicines Agency (EMA) has recommended the approval of Vamorolone, the first ever treatment for all patients with Duchenne muscular dystrophy (DMD)....

Alex’s Wish attends Health & Technology Workshop

September 16, 2016 12:21 pm

We were delighted to attend a workshop organised by Duchenne UK this week in London. The workshop was designed to understand the Health Technology Assessment (HTA) process in England, and to give an overview of health economics and the process of new drug approval and how the Duchenne community can come together to bring new drugs to market as quickly as possible....